Status | Study |
Active, not recruiting |
Study Name: An Open-Label, Intrapatient, Dose-Escalation Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of ALXN1210 Administered Intravenously to Patients With Paroxysmal Nocturnal Hemoglobinuria Condition: Paroxysmal Nocturnal Hemoglobinuria (PNH) Date: 2015-11-02 Interventions: Biological: Study Drug - ALXN1210 |
Recruiting |
Study Name: Pilot Study to Assess Safety, Preliminary Efficacy and Pharmacokinetics of S.C. APL-2 in PNH Subjects Condition: Paroxysmal Nocturnal Hemoglobinuria Date: 2015-10-27 Interventions: Drug: APL-2 |
Recruiting |
Study Name: Coversin in Paroxysmal Nocturnal Haemoglobinuria (PNH) Condition: Paroxysmal Nocturnal Haemoglobinuria (PNH) Date: 2015-09-10 Interventions: Drug: Coversin Patients enrolled in this protocol will initially be treated with an ablating dose of Cov |
Recruiting |
Study Name: Proof of Concept Study to Assess the Efficacy, Safety and Pharmacokinetics of LFG316 in Patients With Paroxysmal Nocturnal Hemoglobinuria Condition: Paroxysmal Nocturnal Hemoglobinuria PNH Date: 2015-08-07 Interventions: Biological: LFG316 LFG316 will be administered to all patients enrolled in the study |
Active, not recruiting |
Study Name: A Phase 1/2 Study of an Investigational Drug, ALN-CC5, in Healthy Adult Volunteers and Patients With PNH Condition: Paroxysmal Nocturnal Hemoglobinuria (PNH) Date: 2015-01-23 Interventions: Drug: ALN-CC5 Single or multip |
Active, not recruiting |
Study Name: A Phase I Study to Assess the Safety APL-2 as an Add-On to Standard of Care in Subjects With PNH Condition: Paroxysmal Nocturnal Hemoglobinuria (PNH) Date: 2014-10-08 Interventions: Drug: APL-2 |
Active, not recruiting |
Study Name: Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Classic Paroxysmal Nocturnal Hemoglobinuria Condition: Paroxysmal Nocturnal Hemoglobinuria Hemoglobinuria Date: 2012-07-14 Interventions: Drug: Levamisole+cyclosporin A+Glucocorticoids |
Completed |
Study Name: Paroxysmal Nocturnal Hemoglobinuria Human Anti-Human Antibodies Study Condition: Paroxysmal Nocturnal Hemoglobinuria PNH Date: 2011-08-05 |
Active, not recruiting |
Study Name: Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry Condition: Paroxysmal Nocturnal Hemoglobinuria Date: 2011-04-15 |
Terminated |
Study Name: Safety and Pharmacokinetics of TT30 in Subjects With Paroxysmal Nocturnal Hemoglobinuria (PNH) Condition: Paroxysmal Nocturnal Hemoglobinuria (PNH) Date: 2011-04-12 Interventions: Drug: ALXN1102 Single Ascendin |